After 30 years, scientists finally have a drug for a deadly brain disease

The FDA has approved Zanvastro, the first drug designed to directly treat Alexander disease, a rare and often fatal neurological disorder. Developed through decades of research, clinical trials showed Zanvastro stabilized motor function and improved movement in some patients. This approval covers patients across all age groups and represents a major advance for a condition that previously had no disease-modifying treatment options.